CRISPR-Cas9n-mediated ELANE promoter editing for gene therapy of severe congenital neutropenia

Nasri, Masoud; Ritter, Malte U.; Mir, Perihan; Dannenmann, Benjamin; Kaufmann, Masako M.; Arreba-Tutusaus, Patricia; Xu, Yun; Borbaran-Bravo, Natalia; Klimiankou, Maksim; Lengerke, Claudia; Zeidler, Cornelia; Cathomen, Toni; Welte, Karl; Skokowa, Julia

dc.contributor.author	Nasri, Masoud
dc.contributor.author	Ritter, Malte
dc.contributor.author	Mir, Perihan
dc.contributor.author	Dannenmann, Benjamin
dc.contributor.author	Arreba-Tutusaus, Patricia
dc.contributor.author	Xu, Yun
dc.contributor.author	Borbaran-Bravo, Natalia
dc.contributor.author	Klimiankou, Maksim
dc.contributor.author	Lengerke, Claudia
dc.contributor.author	Zeidler, Cornelia
dc.contributor.author	Welte, Karl
dc.contributor.author	Skokowa, Julia
dc.date.accessioned	2025-01-22T15:09:14Z
dc.date.available	2025-01-22T15:09:14Z
dc.date.issued	2024
dc.identifier.issn	1525-0016
dc.identifier.uri	http://hdl.handle.net/10900/160562
dc.language.iso	en	en
dc.publisher	Cambridge : Cell Press	de_DE
dc.relation.uri	http://dx.doi.org/10.1016/j.ymthe.2024.03.037
dc.subject.ddc	570	de_DE
dc.subject.ddc	610	de_DE
dc.title	CRISPR-Cas9n-mediated ELANE promoter editing for gene therapy of severe congenital neutropenia	de_DE
dc.type	Article	de_DE
utue.quellen.id	20241001000000_01213
utue.publikation.seiten	1628-1642	de_DE
utue.personen.roh	Nasri, Masoud
utue.personen.roh	Ritter, Malte U.
utue.personen.roh	Mir, Perihan
utue.personen.roh	Dannenmann, Benjamin
utue.personen.roh	Kaufmann, Masako M.
utue.personen.roh	Arreba-Tutusaus, Patricia
utue.personen.roh	Xu, Yun
utue.personen.roh	Borbaran-Bravo, Natalia
utue.personen.roh	Klimiankou, Maksim
utue.personen.roh	Lengerke, Claudia
utue.personen.roh	Zeidler, Cornelia
utue.personen.roh	Cathomen, Toni
utue.personen.roh	Welte, Karl
utue.personen.roh	Skokowa, Julia
dcterms.isPartOf.ZSTitelID	Molecular Therapy	de_DE
dcterms.isPartOf.ZS-Issue	6	de_DE
dcterms.isPartOf.ZS-Volume	32	de_DE
utue.fakultaet	04 Medizinische Fakultät